False claims of equivalence in the neurosurgical trauma literature: prevalence and associated factors–a systematic review protocol

Protocol and registration

This systematic review and meta-analysis will be reported following the Preferred Reporting Items for Systematic Review and Meta-Analyses guidelines.

Eligibility criteria

Published randomised clinical trials (RCTs) that enrolled only TBI patients and investigated any type of intervention (surgical or non-surgical) will be eligible for inclusion. The following journals were selected for screening based on the impact factor and importance to the neurosurgical trauma literature: New England Journal of Medicine (NEJM); Lancet; Lancet Neurology; Journal of the American Medical Association (JAMA); JAMA Neurology; Journal of Neurology, Neurosurgery and Psychiatry (JNNP); Neurosurgery; Journal of Neurosurgery; Neurosurgical Focus; World Neurosurgery; Acta Neurochirurgica; Journal of Neurotrauma; Intensive Care Medicine; Critical Care; and Neurocritical Care. For RCT with multiple publications, only the reporting of the primary outcome was considered. Considering that randomised clinical trials, compared with other study designs, usually are better planned and conducted, besides being published in journals with more rigorous peer review, we believe these criteria will strengthen our results.

Information sources and search strategy

The MEDLINE/PubMed database will be searched for articles in English published from January 1960 to July 2020. The descriptors (((((Traumatic brain injury[Title/Abstract]) OR (TBI[Title/Abstract])) OR (Brain trauma[Title/Abstract])) OR (Brain concussion[Title/Abstract])) OR (Brain contusion[Title/Abstract])) OR (head trauma[Title/Abstract]) OR (head injury[Title/Abstract]) OR (brain injury[Title/Abstract]) will be used. The filter ‘Randomised clinical trials’ will be applied.

Study selection

The search strategy aims to achieve a sample of RCTs published in the neurosurgical trauma literature from which negative trials could be selected. Negative trials will be defined as those that concluded equivalent outcomes (either dichotomous or continuous) in the treatment arms by explicitly stating it (eg, ‘there was no statistically significant difference between the groups’). Otherwise, positive trials will be used as controls. Only the primary outcome intention to treat analysis will be considered, identified by a clear statement of the authors in the methods section or a clear primary focus of the article. If no clear primary outcome can be identified, the neurological/functional outcome or death, hierarchically, will be considered the outcome of interest. All articles’ titles and abstracts were screened by two authors (ALFOJR and JVMPO) for eligibility. The selected articles will be adjudicated by a third author (DJFS), and disagreements will be resolved by consensus. Additional studies identified in the reference section of the selected articles can be included if the eligibility criteria are fulfilled. No RCT studies, as well as no TBI works, will be excluded.

Data collection and analysis

Data will be abstracted and recorded on a standardised form regarding the following: journal, year of publication, study country (high income or low and middle income), first and last author affiliations (neurosurgery or other), the presence of a statistician among the authors, single-centre or multicentre trial, type of trial design (superiority, non-inferiority or equivalence), the presence of a priori sample size and power calculation, type of TBI (mild, moderate and severe), setting (prehospital or intrahospital), intervention (surgical, drug or other), allocation concealment and blinding, number of patients, follow-up period, the event rates in the two treatment arms, the presence of a post hoc power calculation, the discussion of lack of power as a limitation, funding (industry, independent or none) and conflict of interest (when explicitly stated). The full text of the included articles will be systematically reviewed by two authors (ALFOJR and JVMPO). The interobserver agreement and the κ-statistic will be calculated. Disagreements will be resolved by a third author (DJFS). The data analysis will be blinded to the authors and institutions of the study.

The primary outcome will be the prevalence of false claim of equivalence in neurosurgical literature. A false claim of equivalence will be identified by insufficient power to detect a clinically meaningful effect, which will be defined under two scenarios for each type of outcome as follows: for categorical outcomes, a difference of at least 25% and 50% between the two groups given the control group baseline event rate, and for continuous outcomes, a Cohen’s d of at least 0.5 and 0.8 (between groups) given the control group outcome values. Using the number of patients in each treatment arm and the minimum effect sizes to be detected, the power of each study will be calculated with the assumption of a two-tailed alpha that equals 0.05.

Traditional descriptive statistics will be used to present the included RCT characteristics. Standardised differences between the groups with and without a false claim of equivalence will be calculated as proposed by Yang and Dalton.13 The variables with a standardised difference equal or above 0.2 and 0.5 will be considered weakly and strongly associated with false claims of equivalence, respectively. All analyses will be conducted with the SPSS software (IBM Corp. SPSS Statistics for Windows, V.24.0. Armonk, NY).

Risk of bias in individual studies

The entire text of each included paper will be evaluated in a structured fashion for prespecified attributes. The second version of the Cochrane risk-of-bias tool (RoB 2) for randomised trials will be used.14 RoB 2 is structured into a fixed set of domains of bias, focusing on different aspects of trial design, conduct and reporting. Within each domain, a series of questions (signalling questions) aim to elicit information about features of the trial that are relevant to risk of bias. A proposed judgement about the risk of bias arising from each domain is generated by an algorithm, based on answers to the signalling questions. Judgement can be ‘low’ or ‘high’ risk of bias or can express ‘some concerns’.

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